CMT Research Foundation

08/11/2026

A recent study found that a drug that helps other nerve diseases makes CMT4B1 worse, and figuring out why has opened a more promising path toward treatment, including a possible path forward for the related subtype CMT4B2.

This work was funded jointly by the Muscular Dystrophy Association and the CMT Research Foundation.

Read "Project Report: A Negative Result Points to the Way Forward in CMT4B", and other CMTRF Funded Research articles from the CMT Research Foundation.

08/07/2026

Curious about the 2026 Global CMT Research Convention and missed the preview webinar? Watch it now!

Charcot-Marie-Tooth disease drug development is at a pivotal moment...

08/05/2026

With one voice, organizations spanning the Charcot-Marie-Tooth community, together with input from partners across the field, are speaking up together--promoting a new framework for CMT clinical trials.

The CMT Research Foundation is proud to join the Muscular Dystrophy Association, Charcot-Marie-Tooth Association, Hereditary Neuropathy Foundation, and The Hunt to Cure CMT4B3 to unveil new consensus recommendations for CMT clinical trials.

This shared framework gives researchers a common roadmap, one that should make it easier to design, run, and interpret CMT trials going forward.

https://cmtrf.org/cmt-orgs-come-together-to-advocate-for-new-clinical-trial-framework/

Read "CMT Orgs Come together to Advocate for New Clinical Trial Framework", and other CMT Research Updates articles from the CMT Research Foundation.

08/04/2026

You can contribute to CMT research today, just by planning for the future.

Read "The Promise Society: A New Way to Support CMT Research", and other Foundation News articles from the CMT Research Foundation.

08/04/2026

Interested in the Global CMT Research Convention in September? We've got a webinar coming up on August 6th to break down reasons you should consider going. Register for the webinar today!

https://events.zoom.us/ev/AppT771cweCLb1RyKkak2TUTMIHOlulJa4S3NXpBB9QjRg3xHZbY~Asb6VBmwH1pKd7s7kP2S6vkf0ZWCc_E6D0fZEmPLz3KBKwQZksrll6yrWw

07/30/2026

Thinking about attending the 2026 Global CMT Research Convention? Our CEO Laura MacNeill explains what you can get out of it.

If you're still on the fence, we'll talk through what the convention has to offer and answer any of your questions during our August 6th Convention Preview Webinar.

REGISTER FOR THE WEBINAR NOW: https://events.zoom.us/ev/AppT771cweCLb1RyKkak2TUTMIHOlulJa4S3NXpBB9QjRg3xHZbY~Asb6VBmwH1pKd7s7kP2S6vkf0ZWCc_E6D0fZEmPLz3KBKwQZksrll6yrWw

07/30/2026

Happy Birthday to our Founder and Chief Mission Officer, Susan Ruediger! 🎉

Your vision has helped fuel nearly $30 million in research, support 36+ projects, and move 6 treatments into or toward clinical trials.

Here’s to another year of changing lives. Happy Birthday, Susan!

07/28/2026

Want to learn more about the 2026 Global CMT Research Convention? Register for our Behind the Scenes preview webinar on August 6th!

https://events.zoom.us/e/view/preview/K5RkkYgzTeaTwLYKaQSwyw

07/22/2026

If you're thinking about joining us for the 2026 Global CMT Research Convention (September 24-26, Cambridge, MA), you should come get a preview of what to expect! Plus, you'll get a chance to ask any questions you might have about attending.

Register today for our August 6th Webinar giving a behind-the-scenes look at the convention.

Read "WEBINAR: Behind the Scenes, 2026 Global CMT Research Convention Preview", and other Foundation News articles from the CMT Research Foundation.

07/21/2026

The CMT Research Foundation, in partnership with the 1J Foundation, has funded a new study at the University of Miami led by Dr. Stephan Zuchner to evaluate a newly-identified genetic variant linked to Charcot-Marie-Tooth disease type 1J and to test whether a targeted genetic medicine can address it.

Read "Taking Aim at CMT1J with a genetic medicine", and other CMTRF Funded Research articles from the CMT Research Foundation.